Gene Therapy

Combinining gene therapy and medical device makes progress in RP

Investigators who are examining end-stage disease see significant visual recovery in 2 patients.

Gene therapy trial highlights RPGR-associated X-linked RP

The therapy offers improved retinal sensitivity, visual function, as well as improvements in mobility.

Combining gene therapy and medical device makes progress in RP

Investigators who are examining end-stage disease see significant visual recovery in 2 patients.

UCI-led report illustrates potential of precision genome editing in treating inherited retinal diseases

October 13, 2022

According to University of California, Irvine researchers, current preclinical successes and clinical genome editing approaches for treating inherited retinal degenerative disease and stresses there is hope that in vivo gene editing will be the future treatment paradigm for these diseases.

Nanoscope Therapeutics receives fast track designation from FDA for MCO-010 for treatment of retinitis pigmentosa

October 12, 2022

Nanoscope Therapeutics Inc. announced the FDA has granted Fast Track Designation to MCO-010, an ambient-light activatable multi-characteristic opsin optogenetic monotherapy to restore vision in blind patients, for the treatment of retinitis pigmentosa via intravitreal injection.