Gene Therapy

Leber hereditary optic neuropathy: Outlining disease’s natural course

A new gene therapy for this patient population targets the ND4 gene mutation.

Investigators explore pathogenic cytokines as biomarkers for DME

BIGH3 is an extracellular matrix protein that can act in an autocrine, paracrine manner.

Gyroscope Therapeutics, UPenn to develop gene therapies for serious eye diseases

Two teams of researchers from Gyroscope Therapeutics and the University of Pennsylvania are joining forces to explore gene therapy targets for three specific serious eye diseases.

Collaboration formed to develop AAV-based gene therapies for eye disease

January 06, 2021

ViGeneron and Biogen this week have announced a global collaboration and licensing agreement in which the partners will develop and commercialize gene therapy products based on adeno-associated virus (AAV) vectors that treat inherited eye disease.