
A successful Type B Rare Disease Evidence Principles meeting confirms the pivotal study design, opening a potential BLA pathway on 6-month efficacy data, with dosing expected to begin in the fourth quarter of 2026.
In this episode of EyePod, David Hutton sits down with Neena Haider, PhD, and Arun Upadhyay, PhD, to talk about modifier gene therapy.
In this episode of EyePod, David Hutton sits down with Neena Haider, PhD, and Arun Upadhyay, PhD, to talk about modifier gene therapy.




